Amino Acid Disorders
- PKU (Phenylketonuria)
 - Hyperphenylalaninaemia
 - Tyrosinaemia
 - Homocystinuria
 - MSUD (Maple Syrup Urine Disease)
 - Gyrate Atrophy
 
Organic Acidaemias
- Propionic Acidaemia
 - Methlymalonic Acidaemia
 - Isovaleric Acidaemia
 - Glutaric Acidaemia Type 1
 
Urea Cycle Disorders
- Ornithine transcarbamylase deficiency (OTC)
 - Carbamylphosphate synthase 1 deficiency (CPS 1)
 - Citrullinaemia
 - Arginosuccinic aciduria
 - Argininaemia
 - HHH Syndrome (Hyperammonaemia, hyperornithinaemia, homocitrullinuria)
 
Disorders of fatty acid oxidation and ketogenesis
- Carnitine palmitoyltransferase 1 deficiency (CPT 1)
 - Carnitine palmitoyltransferase 2 deficiency (CPT 2)
 - Very long chain acyl-CoA dehydrogenase deficiency (VLCAD)
 - Long chain acyl-CoA dehydrogenase deficiency (LCHAD)
 - Medium chain acyl-CoA dehydrogenase deficiency (MCAD)
 - Short chain acyl-CoA dehydrogenase deficiency (SCAD)
 - Glutaric Acidaemia Type 2 (MADD)
 - HMG-CoA lyase deficiency
 
Carbohydrate Disorders
- Hereditary Fructose intolerance (Fructosaemia)
 - Galactosaemia
 - Glycogen Storage Disorder Type 1 (von Gierke)
 - Glycogen Storage Disorder Type 2 (Pompe/Acid Maltase Deficiency)
 - Glycogen Storage Disorder Type 3 (Cori / Forbes)
 
Lysosomal Storage Disorders (LSD)
- MPS Type 1 (Hurler Scheie, Hurler, Scheie)
 - MPS Type 2 (Hunter)
 - MPS Type 3 (Sanfilippo)
 - MPS Type 4 (Morquio)
 - MPS Type 6 (Maroteaux-Lamy)
 - MPS Type 7 (Sly)
 - MPS Type 9 (Natowicz)
 - Niemann-Pick disease Type1 and Type 2
 - Gaucher disease
 - Fabry disease
 
Peroxisomal Disorders
- X-linked ALD (Adrenoleukodystrophy)
 - AMN (Adrenomyeloneuropathy)
 - Refsum Disease
 - Zellweger syndrome
 
Mitochondrial disorders
- MELAS (Encephalomyopathy, lactic acidosis, stroke-like episodes, small stature, migraine, diabetes mellitus)
 - MERRF (Myoclonic Epilepsy, ragged red fibres)
 - NARP (Neuropathy, ataxia, retinitis pigmentosa)
 
Others
- TMAU (Trimethylaminuria/Fish odour syndrome)
 - SLO (Smith-Lemli-Opitz syndrome)
 - Alkaptonuria
 
Last reviewed: 05 September 2024